Duchenne muscular dystrophy families are sharing stories about Elevidys complications on social media. But they aren’t ...

The death of a boy with Duchenne muscular dystrophy, tied to a gene therapy, is above all a tragedy. But it is also ...

CSL Behring’s Andembry is now approved as a subcutaneous, self-injection for hereditary angioedema (HAE) patients ages 12 and older and will be available by the end of June 2025.

President Javier Milei's severe budget cuts to Argentina's public health system have led to a decline in care, particularly affecting cancer patients, according to experts, government workers and ...