Eleven-year-old Matthew from Enniskillen, UK, made history in 2013 when he became one of the first in the world to receive gene therapy for adrenoleukodystrophy (ALD). As the Gene Therapy Program celebrates its 10-year anniversary, we also celebrate Matthew’s many milestones: http://ms.spr.ly/6184VwsEA | Boston Children’s Hospital

48K views · 564 reactions | Doctors in Philadelphia have successfully used a custom Crispr gene-editing therapy to treat a newborn with a rare and life-threatening genetic disorder. Subscribe to our newsletter at the #linkinbio for the full story. | 1440 | Facebook